Terapia genética com valoctocogene roxaparvovec para hemofilia A.
22 Mar, 2022 | 11:28hValoctocogene Roxaparvovec Gene Therapy for Hemophilia A – New England Journal of Medicine (link para o resumo – $ para o texto completo)
Comentários:
Valoctocogene Roxaparvovec Evaluated in Severe Hemophilia A – HealthDay
Hemophilia A Gene Therapy Reduced Bleeding Events, Need for Clotting Factors – AJMC